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148 results
Topics : Diseases and conditions
Topics : Congenital, genetic and rare diseases
Date : du 03/10/2017 au 03/10/2021
Language : Français
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Practice guidelines and other guides
- 1 result
Inborn errors of metabolism : assessment of expanded newborn screening using tandem mass spectrometry in France (part 2)
Public Health guideline
- Posted on 3/2/2020
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Drugs, devices and medical acts
- 147 results
EVRYSDI (risdiplam)
Medicine
- Posted on 30/9/2021
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OXLUMO (lumasiran)
Medicine
- Posted on 24/9/2021
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ELZONRIS (tagraxofusp)
Medicine
- Posted on 26/8/2021
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COAGADEX (facteur X de coagulation humain)
Medicine
- Posted on 24/9/2021
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REBLOZYL (luspatercept)
Medicine
- Posted on 25/1/2024
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FINTEPLA (fenfluramine)
Medicine
- Posted on 3/6/2021
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ADAKVEO (crizanlizumab)
Medicine
- Posted on 7/5/2021
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ISTURISA (osilodrostat)
Medicine
- Posted on 7/5/2021
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LIBMELDY 2-10 x 106 cellules/ml dispersion pour perfusion (atidarsagène autotemcel)
Medicine
- Posted on 20/10/2022
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XROMI (hydroxycarbamide)
Medicine
- Posted on 9/4/2021
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See 147 result in Drugs, devices and medical acts
Français
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