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17 results
Topics : Congenital, genetic and rare diseases
Topics : Central nervous system diseases
Type : Drugs, devices and medical acts
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Comparative genomic hybridization array (CGHA) analysis in postnatal context - INAHTA Brief
Health technology assessment
- Posted on 20/07/2023
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Evaluation of the METAglut1™ test in the diagnosis of glucose transporter type 1 deficiency syndrome - INAHTA Brief
Health technology assessment
- Posted on 27/04/2023
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ENSPRYNG (satralizumab)
Medicine
- Posted on 10/02/2022
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ONTOZRY (cénobamate)
Medicine
- Posted on 28/06/2023
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EVRYSDI (risdiplam)
Medicine
- Posted on 30/09/2021
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FINTEPLA (fenfluramine)
Medicine
- Posted on 03/06/2021
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LIBMELDY 2-10 x 106 cellules/ml dispersion pour perfusion (atidarsagène autotemcel)
Medicine
- Posted on 20/10/2022
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ZOLGENSMA (onasemnogene abeparvovec)
Medicine
- Posted on 25/05/2023
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LAMICTAL - LAMICSTART (lamotrigine)
Medicine
- Posted on 07/03/2022
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INOVELON (rufinamide)
Medicine
- Posted on 25/11/2019 - Mis à jour le 25/11/2019
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