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165 results
Type : Drugs, devices and medical acts
Topics : Congenital, genetic and rare diseases
Language : Français
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Date
VYVGART (efgartigimod alfa)
Medicine
- Posted on 01/08/2024 - Mis à jour le 1/8/2024
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CAMZYOS (mavacamten)
Medicine
- Posted on 09/11/2023
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ENJAYMO (sutimlimab)
Medicine
- Posted on 08/09/2023
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POMBILITI (cipaglucosidase alfa)
Medicine
- Posted on 09/11/2023
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Comparative genomic hybridization array (CGHA) analysis in postnatal context - INAHTA Brief
Health technology assessment
- Posted on 20/07/2023
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document
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Evaluation of the METAglut1™ test in the diagnosis of glucose transporter type 1 deficiency syndrome - INAHTA Brief
Health technology assessment
- Posted on 27/04/2023
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document
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CEVENFACTA (eptacog bêta - FVIIa)
Medicine
- Posted on 27/01/2023
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AMVUTTRA (vutrisiran)
Medicine
- Posted on 05/04/2024
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EVKEEZA (évinacumab)
Medicine
- Posted on 06/05/2024
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FILSUVEZ (extrait sec raffiné d’écorce de bouleau)
Medicine
- Posted on 03/02/2023
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