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162 results
Topics : Congenital, genetic and rare diseases
Type : Drugs, devices and medical acts
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ULTOMIRIS
Medicine
- Posted on 29/04/2024
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JORVEZA
Medicine
- Posted on 15/09/2020
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SPINRAZA
Medicine
- Posted on 02/09/2020
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PROLASTIN
Medicine
- Posted on 08/03/2024
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SCENESSE
Medicine
- Posted on 01/10/2020
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MEPSEVII
Medicine
- Posted on 01/07/2020 - Mis à jour le 1/7/2020
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GIVLAARI
Medicine
- Posted on 01/04/2021
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BENLYSTA
Medicine
- Posted on 04/02/2022
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KALYDECO
Medicine
- Posted on 10/01/2024
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SYMKEVI / KALYDECO
Medicine
- Posted on 06/10/2021
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IMBRUVICA
Medicine
- Posted on 13/04/2023
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Nasal nitric oxide (NO) measurement as a diagnostic test for primary ciliary dyskinesia (PCD) - INAHTA Brief
Health technology assessment
- Posted on 16/09/2020
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document
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CREON (pancréatine)
Medicine
- Posted on 18/03/2020 - Mis à jour le 18/3/2020
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CUFENCE (trientine dichlorhydrate)
Medicine
- Posted on 25/01/2024
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WAYLIVRA (volanesorsen)
Medicine
- Posted on 12/03/2020
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REVOLADE (eltrombopag)
Medicine
- Posted on 04/03/2020 - Mis à jour le 4/3/2020
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LAMICTAL - LAMICSTART (lamotrigine)
Medicine
- Posted on 07/03/2022
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ONPATTRO
Medicine
- Posted on 22/01/2020 - Mis à jour le 22/1/2020
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MABTHERA
Medicine
- Posted on 27/04/2023
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HUMIRA
Medicine
- Posted on 11/04/2023
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NAMUSCLA
Medicine
- Posted on 29/03/2021
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HEMLIBRA
Medicine
- Posted on 22/04/2024
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EZETROL (ézétimibe)
Medicine
- Posted on 09/12/2019 - Mis à jour le 9/12/2019
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COLOBREATHE (colistiméthate de sodium)
Medicine
- Posted on 09/12/2019 - Mis à jour le 9/12/2019
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INOVELON (rufinamide)
Medicine
- Posted on 25/11/2019 - Mis à jour le 25/11/2019
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CLAIRYG (immunoglobuline humaine normale/ immunoglobuline humaine normale (plas...)
Medicine
- Posted on 06/03/2024
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ILARIS
Medicine
- Posted on 08/12/2020
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TEGSEDI
Medicine
- Posted on 30/09/2019
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LUXTURNA
Medicine
- Posted on 03/08/2023
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ROACTEMRA
Medicine
- Posted on 23/02/2022
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MYALEPTA (métréleptine)
Medicine
- Posted on 07/06/2019 - Mis à jour le 12/6/2019
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KINERET
Medicine
- Posted on 02/12/2020
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SIGNIFOR (pasiréotide)
Medicine
- Posted on 12/03/2019 - Mis à jour le 12/6/2019
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CUPRIOR (trientine (tétrachlorhydrate de))
Medicine
- Posted on 11/06/2019 - Mis à jour le 12/6/2019
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RUCONEST (conestat alpha)
Medicine
- Posted on 31/03/2021
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CRYSVITA
Medicine
- Posted on 25/01/2024
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