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162 results
Type : Medicine
Topics : Congenital, genetic and rare diseases
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(162)
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ADAKVEO (crizanlizumab)
Medicine
- Posted on 07/05/2021
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ADCETRIS
Medicine
- Posted on 29/03/2023
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ALDURAZYME (laronidase)
Medicine
- Posted on 04/02/2022
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ALFALASTIN (alpha-1 antitrypsine humaine)
Medicine
- Posted on 01/06/2017 - Mis à jour le 12/6/2019
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my selection
ALPROLIX (eftrénonacog alfa)
Medicine
- Posted on 10/03/2017 - Mis à jour le 12/6/2019
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AMVUTTRA (vutrisiran)
Medicine
- Posted on 05/04/2024
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ARCOXIA (étoricoxib)
Medicine
- Posted on 27/04/2015 - Mis à jour le 12/6/2019
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AYVAKYT (avapritinib)
Medicine
- Posted on 05/09/2024
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BENLYSTA
Medicine
- Posted on 04/02/2022
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BERINERT (inhibiteur de C1 estérase humaine/ inhibiteur de la C1 estérase humain...)
Medicine
- Posted on 08/02/2019 - Mis à jour le 12/6/2019
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my selection
BESPONSA (inotuzumab ozogamicine)
Medicine
- Posted on 10/10/2022
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BESREMI (ropeginterféron alfa-2b)
Medicine
- Posted on 23/12/2020
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BRINEURA (cerliponase alfa)
Medicine
- Posted on 24/10/2018 - Mis à jour le 12/6/2019
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BRONCHITOL (mannitol)
Medicine
- Posted on 21/05/2013 - Mis à jour le 12/6/2019
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CALCITONINE PHARMY II (calcitonine de saumon)
Medicine
- Posted on 24/12/2019
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CALSYN (calcitonine de saumon)
Medicine
- Posted on 24/12/2019
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CAMZYOS (mavacamten)
Medicine
- Posted on 09/11/2023
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CARBAGLU (acide carglumique)
Medicine
- Posted on 15/05/2014 - Mis à jour le 12/6/2019
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CAYSTON (aztréonam lysine/ lysine (aztréonam de))
Medicine
- Posted on 02/05/2018 - Mis à jour le 12/6/2019
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CEPROTIN (protéine C humaine)
Medicine
- Posted on 03/08/2023
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CERDELGA (éliglustat (tartrate d'))
Medicine
- Posted on 18/01/2016 - Mis à jour le 12/6/2019
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CEVENFACTA (eptacog bêta - FVIIa)
Medicine
- Posted on 27/01/2023
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CHENODEOXYCHOLIC ACID LEADIANT (chénodésoxycholique (acide))
Medicine
- Posted on 28/11/2018 - Mis à jour le 12/6/2019
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CINRYZE (inhibiteur de la C1 estérase humaine)
Medicine
- Posted on 08/02/2019 - Mis à jour le 12/6/2019
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CLAIRYG (immunoglobuline humaine normale/ immunoglobuline humaine normale (plas...)
Medicine
- Posted on 06/03/2024
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COAGADEX (facteur X de coagulation humain)
Medicine
- Posted on 24/09/2021
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COLOBREATHE (colistiméthate de sodium)
Medicine
- Posted on 09/12/2019 - Mis à jour le 9/12/2019
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CREON (pancréatine)
Medicine
- Posted on 18/03/2020 - Mis à jour le 18/3/2020
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CRYSVITA
Medicine
- Posted on 25/01/2024
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CUFENCE (trientine dichlorhydrate)
Medicine
- Posted on 25/01/2024
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CUPRIOR (trientine (tétrachlorhydrate de))
Medicine
- Posted on 11/06/2019 - Mis à jour le 12/6/2019
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CUROSURF (poractant alfa)
Medicine
- Posted on 20/01/2015 - Mis à jour le 12/6/2019
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CYSTADROPS (mercaptamine (chlorhydrate de))
Medicine
- Posted on 04/05/2018 - Mis à jour le 12/6/2019
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DEFITELIO
Medicine
- Posted on 05/10/2021
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DELURSAN (acide ursodésoxycholique)
Medicine
- Posted on 24/10/2018 - Mis à jour le 12/6/2019
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DIDRONEL (étidronate)
Medicine
- Posted on 06/09/2012 - Mis à jour le 12/6/2019
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