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102 results
Topics : Population groups
Topics : Congenital, genetic and rare diseases
Topics : Diagnostic and therapeutic techniques
Type : Drugs, devices and medical acts
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Comparative genomic hybridization array (CGHA) analysis in postnatal context - INAHTA Brief
Health technology assessment
- Posted on 20/07/2023
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Evaluation of the METAglut1™ test in the diagnosis of glucose transporter type 1 deficiency syndrome - INAHTA Brief
Health technology assessment
- Posted on 27/04/2023
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document
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CEVENFACTA (eptacog bêta - FVIIa)
Medicine
- Posted on 27/01/2023
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AMVUTTRA (vutrisiran)
Medicine
- Posted on 05/04/2024
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EVKEEZA (évinacumab)
Medicine
- Posted on 06/05/2024
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FILSUVEZ (extrait sec raffiné d’écorce de bouleau)
Medicine
- Posted on 03/02/2023
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FLUDROCORTISONE ACETATE ACCORD (acétate de fludrocortisone)
Medicine
- Posted on 13/10/2022
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NEXVIADYME (avalglucosidase alfa)
Medicine
- Posted on 12/10/2023
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ENSPRYNG (satralizumab)
Medicine
- Posted on 10/02/2022
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EVRYSDI (risdiplam)
Medicine
- Posted on 30/09/2021
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FINTEPLA (fenfluramine)
Medicine
- Posted on 03/06/2021
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ADAKVEO (crizanlizumab)
Medicine
- Posted on 07/05/2021
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LIBMELDY 2-10 x 106 cellules/ml dispersion pour perfusion (atidarsagène autotemcel)
Medicine
- Posted on 20/10/2022
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XROMI (hydroxycarbamide)
Medicine
- Posted on 09/04/2021
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ESPEROCT (turoctocog alfa pégol)
Medicine
- Posted on 11/03/2021
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ZOLGENSMA (onasemnogene abeparvovec)
Medicine
- Posted on 25/05/2023
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PALYNZIQ (pegvaliase)
Medicine
- Posted on 02/12/2020
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KAFTRIO / KALYDECO
Medicine
- Posted on 17/05/2024
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LUCENTIS
Medicine
- Posted on 19/10/2021
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ULTOMIRIS
Medicine
- Posted on 01/07/2024
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TAKHZYRO (lanadélumab)
Medicine
- Posted on 05/03/2024
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SPINRAZA
Medicine
- Posted on 10/07/2024
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TRECONDI
Medicine
- Posted on 05/09/2024
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MEPSEVII
Medicine
- Posted on 01/07/2020 - Mis à jour le 1/7/2020
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GIVLAARI
Medicine
- Posted on 01/04/2021
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BENLYSTA
Medicine
- Posted on 04/02/2022
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KALYDECO
Medicine
- Posted on 10/01/2024
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SYMKEVI / KALYDECO
Medicine
- Posted on 06/10/2021
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CREON (pancréatine)
Medicine
- Posted on 18/03/2020 - Mis à jour le 18/3/2020
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CUFENCE (trientine dichlorhydrate)
Medicine
- Posted on 25/01/2024
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REVOLADE (eltrombopag)
Medicine
- Posted on 04/03/2020 - Mis à jour le 4/3/2020
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LAMICTAL - LAMICSTART (lamotrigine)
Medicine
- Posted on 07/03/2022
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MABTHERA
Medicine
- Posted on 27/04/2023
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HUMIRA
Medicine
- Posted on 18/09/2024
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HEMLIBRA
Medicine
- Posted on 22/04/2024
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EZETROL (ézétimibe)
Medicine
- Posted on 09/12/2019 - Mis à jour le 9/12/2019
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