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54 results
Type : Medicine
Topics : Metabolic diseases
Topics : Congenital, genetic and rare diseases
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acide carglumique
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alglucosidase alfa
(1)
alpha-1 antitrypsine humaine
(2)
atorvastatine calcique
(1)
calcitonine de saumon
(3)
canakinumab
(1)
icatibant
(1)
idursulfase
(1)
laronidase
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miglustat
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nitisinone
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simvastatine
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somatropine
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tocofersolan
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POMBILITI (cipaglucosidase alfa)
Medicine
- Posted on 09/11/2023
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AMVUTTRA (vutrisiran)
Medicine
- Posted on 05/04/2024
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EVKEEZA (évinacumab)
Medicine
- Posted on 06/05/2024
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NEXVIADYME (avalglucosidase alfa)
Medicine
- Posted on 12/10/2023
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OXLUMO (lumasiran)
Medicine
- Posted on 24/09/2021
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PALYNZIQ (pegvaliase)
Medicine
- Posted on 02/12/2020
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VYNDAQEL
Medicine
- Posted on 16/10/2020 - Mis à jour le 16/10/2020
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MIACALCIC
Medicine
- Posted on 02/10/2020 - Mis à jour le 2/10/2020
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PROLASTIN
Medicine
- Posted on 08/03/2024
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MEPSEVII
Medicine
- Posted on 01/07/2020 - Mis à jour le 1/7/2020
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