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72 results
Topics : Endocrine system and metabolic diseases
Topics : Congenital, genetic and rare diseases
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Practice guidelines and other guides
- 2 results
Clinical and economic assessment of screening for HFE1 haemochromatosis in 2004
Public Health guideline
- Posted on 1/4/2004 - Mis à jour le 12/12/2006
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Management of patients with HFE-related haemochromatosis (Type 1 haemochromatosis)
Practice guidelines
- Posted on 1/7/2005 - Mis à jour le 26/9/2006
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Drugs, devices and medical acts
- 70 results
POMBILITI (cipaglucosidase alfa)
Medicine
- Posted on 9/11/2023
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Evaluation of the METAglut1™ test in the diagnosis of glucose transporter type 1 deficiency syndrome - INAHTA Brief
Health technology assessment
- Posted on 27/4/2023
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AMVUTTRA (vutrisiran)
Medicine
- Posted on 5/4/2024
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EVKEEZA (évinacumab)
Medicine
- Posted on 6/5/2024
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FLUDROCORTISONE ACETATE ACCORD (acétate de fludrocortisone)
Medicine
- Posted on 13/10/2022
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NEXVIADYME (avalglucosidase alfa)
Medicine
- Posted on 12/10/2023
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TECEOS (butédronate)
Medicine
- Posted on 29/7/2022
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OXLUMO (lumasiran)
Medicine
- Posted on 24/9/2021
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ISTURISA (osilodrostat)
Medicine
- Posted on 7/5/2021
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PALYNZIQ (pegvaliase)
Medicine
- Posted on 2/12/2020
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See 70 result in Drugs, devices and medical acts
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