175 results

Topics : Congenital, genetic and rare diseases

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Newborn screening for spinal muscular atrophy_Advance assessment of extension of screening to the general population in France

Public Health guideline - Posted on 10/7/2024

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Acquired and inherited aplastic anemia

Chronic disease guide - Posted on 4/5/2024

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Inborn errors of metabolism : assessment of expanded newborn screening using tandem mass spectrometry in France (part 2)

Public Health guideline - Posted on 3/2/2020

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See 10 result in Practice Guidelines and Other Guides

LIBMELDY 2-10 x 106 cellules/ml dispersion pour perfusion (atidarsagène autotemcel)

Medicine - Posted on 6/10/2023 - Mis à jour le 24/9/2024

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VYVGART (efgartigimod alfa)

Medicine - Posted on 1/8/2024 - Mis à jour le 1/8/2024

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CAMZYOS (mavacamten)

Medicine - Posted on 9/11/2023

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See 165 result in Drugs, devices and medical acts