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165 results
Type : Drugs, devices and medical acts
Topics : Congenital, genetic and rare diseases
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Title
Date
VYVGART (efgartigimod alfa)
Medicine
- Posted on 01/08/2024 - Mis à jour le 1/8/2024
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CAMZYOS (mavacamten)
Medicine
- Posted on 09/11/2023
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ENJAYMO (sutimlimab)
Medicine
- Posted on 08/09/2023
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POMBILITI (cipaglucosidase alfa)
Medicine
- Posted on 09/11/2023
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Comparative genomic hybridization array (CGHA) analysis in postnatal context - INAHTA Brief
Health technology assessment
- Posted on 20/07/2023
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document
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Evaluation of the METAglut1™ test in the diagnosis of glucose transporter type 1 deficiency syndrome - INAHTA Brief
Health technology assessment
- Posted on 27/04/2023
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document
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my selection
CEVENFACTA (eptacog bêta - FVIIa)
Medicine
- Posted on 27/01/2023
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AMVUTTRA (vutrisiran)
Medicine
- Posted on 05/04/2024
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EVKEEZA (évinacumab)
Medicine
- Posted on 06/05/2024
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FILSUVEZ (extrait sec raffiné d’écorce de bouleau)
Medicine
- Posted on 03/02/2023
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FLUDROCORTISONE ACETATE ACCORD (acétate de fludrocortisone)
Medicine
- Posted on 13/10/2022
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my selection
NEXVIADYME (avalglucosidase alfa)
Medicine
- Posted on 12/10/2023
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TECEOS (butédronate)
Medicine
- Posted on 29/07/2022
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my selection
ENSPRYNG (satralizumab)
Medicine
- Posted on 10/02/2022
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ORLADEYO (dichlorhydrate de bérotralstat)
Medicine
- Posted on 08/12/2021
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my selection
ONTOZRY (cénobamate)
Medicine
- Posted on 28/06/2023
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EVRYSDI (risdiplam)
Medicine
- Posted on 30/09/2021
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OXLUMO (lumasiran)
Medicine
- Posted on 24/09/2021
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ELZONRIS (tagraxofusp)
Medicine
- Posted on 26/08/2021
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COAGADEX (facteur X de coagulation humain)
Medicine
- Posted on 24/09/2021
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REBLOZYL (luspatercept)
Medicine
- Posted on 25/01/2024
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FINTEPLA (fenfluramine)
Medicine
- Posted on 03/06/2021
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ADAKVEO (crizanlizumab)
Medicine
- Posted on 07/05/2021
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ISTURISA (osilodrostat)
Medicine
- Posted on 07/05/2021
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LIBMELDY 2-10 x 106 cellules/ml dispersion pour perfusion (atidarsagène autotemcel)
Medicine
- Posted on 20/10/2022
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my selection
XROMI (hydroxycarbamide)
Medicine
- Posted on 09/04/2021
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AYVAKYT (avapritinib)
Medicine
- Posted on 05/09/2024
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ESPEROCT (turoctocog alfa pégol)
Medicine
- Posted on 11/03/2021
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BESREMI (ropeginterféron alfa-2b)
Medicine
- Posted on 23/12/2020
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ZOLGENSMA (onasemnogene abeparvovec)
Medicine
- Posted on 25/05/2023
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PALYNZIQ (pegvaliase)
Medicine
- Posted on 02/12/2020
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KAFTRIO / KALYDECO
Medicine
- Posted on 17/05/2024
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VYNDAQEL
Medicine
- Posted on 16/10/2020 - Mis à jour le 16/10/2020
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LUCENTIS
Medicine
- Posted on 19/10/2021
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SYLVANT
Medicine
- Posted on 02/10/2020 - Mis à jour le 2/10/2020
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MIACALCIC
Medicine
- Posted on 02/10/2020 - Mis à jour le 2/10/2020
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ADCETRIS
Medicine
- Posted on 29/03/2023
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ULTOMIRIS
Medicine
- Posted on 01/07/2024
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TAKHZYRO (lanadélumab)
Medicine
- Posted on 05/03/2024
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JORVEZA
Medicine
- Posted on 15/09/2020
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SPINRAZA
Medicine
- Posted on 10/07/2024
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TRECONDI
Medicine
- Posted on 05/09/2024
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PROLASTIN
Medicine
- Posted on 08/03/2024
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SCENESSE
Medicine
- Posted on 01/10/2020
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MEPSEVII
Medicine
- Posted on 01/07/2020 - Mis à jour le 1/7/2020
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GIVLAARI
Medicine
- Posted on 01/04/2021
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BENLYSTA
Medicine
- Posted on 04/02/2022
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KALYDECO
Medicine
- Posted on 10/01/2024
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SYMKEVI / KALYDECO
Medicine
- Posted on 06/10/2021
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IMBRUVICA
Medicine
- Posted on 13/04/2023
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Nasal nitric oxide (NO) measurement as a diagnostic test for primary ciliary dyskinesia (PCD) - INAHTA Brief
Health technology assessment
- Posted on 16/09/2020
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document
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CREON (pancréatine)
Medicine
- Posted on 18/03/2020 - Mis à jour le 18/3/2020
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CUFENCE (trientine dichlorhydrate)
Medicine
- Posted on 25/01/2024
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my selection
WAYLIVRA (volanesorsen)
Medicine
- Posted on 12/03/2020
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my selection
REVOLADE (eltrombopag)
Medicine
- Posted on 04/03/2020 - Mis à jour le 4/3/2020
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my selection
LAMICTAL - LAMICSTART (lamotrigine)
Medicine
- Posted on 07/03/2022
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my selection
ONPATTRO
Medicine
- Posted on 22/01/2020 - Mis à jour le 22/1/2020
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MABTHERA
Medicine
- Posted on 27/04/2023
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my selection
HUMIRA
Medicine
- Posted on 18/09/2024
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NAMUSCLA
Medicine
- Posted on 29/03/2021
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my selection
HEMLIBRA
Medicine
- Posted on 22/04/2024
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EZETROL (ézétimibe)
Medicine
- Posted on 09/12/2019 - Mis à jour le 9/12/2019
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my selection
COLOBREATHE (colistiméthate de sodium)
Medicine
- Posted on 09/12/2019 - Mis à jour le 9/12/2019
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my selection
INOVELON (rufinamide)
Medicine
- Posted on 25/11/2019 - Mis à jour le 25/11/2019
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my selection
CLAIRYG (immunoglobuline humaine normale/ immunoglobuline humaine normale (plas...)
Medicine
- Posted on 06/03/2024
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ILARIS
Medicine
- Posted on 18/09/2024
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TEGSEDI
Medicine
- Posted on 30/09/2019
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LUXTURNA
Medicine
- Posted on 05/09/2024
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ROACTEMRA
Medicine
- Posted on 18/09/2024
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MYALEPTA (métréleptine)
Medicine
- Posted on 07/06/2019 - Mis à jour le 12/6/2019
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KINERET
Medicine
- Posted on 18/09/2024
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my selection
SIGNIFOR (pasiréotide)
Medicine
- Posted on 12/03/2019 - Mis à jour le 12/6/2019
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CUPRIOR (trientine (tétrachlorhydrate de))
Medicine
- Posted on 11/06/2019 - Mis à jour le 12/6/2019
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my selection
RUCONEST (conestat alpha)
Medicine
- Posted on 31/03/2021
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CRYSVITA
Medicine
- Posted on 25/01/2024
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LAMZEDE (velmanase alfa)
Medicine
- Posted on 08/06/2022
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RESPREEZA (alpha-1 antitrypsine humaine)
Medicine
- Posted on 12/12/2018 - Mis à jour le 12/6/2019
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my selection
ORKAMBI
Medicine
- Posted on 15/04/2024
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MERONEM (méropénem trihydraté)
Medicine
- Posted on 30/11/2018 - Mis à jour le 12/6/2019
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REPATHA
Medicine
- Posted on 18/04/2024
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my selection
RYDAPT
Medicine
- Posted on 04/03/2021
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my selection
BERINERT (inhibiteur de C1 estérase humaine/ inhibiteur de la C1 estérase humain...)
Medicine
- Posted on 08/02/2019 - Mis à jour le 12/6/2019
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my selection
FIRAZYR (icatibant (acétate d'))
Medicine
- Posted on 08/02/2019 - Mis à jour le 12/6/2019
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CINRYZE (inhibiteur de la C1 estérase humaine)
Medicine
- Posted on 08/02/2019 - Mis à jour le 12/6/2019
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HIZENTRA (immunoglobuline humaine normale (plasmatique))
Medicine
- Posted on 07/06/2022
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PROCYSBI (mercaptamine (bitartrate de))
Medicine
- Posted on 29/08/2018 - Mis à jour le 12/6/2019
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my selection
CHENODEOXYCHOLIC ACID LEADIANT (chénodésoxycholique (acide))
Medicine
- Posted on 28/11/2018 - Mis à jour le 12/6/2019
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FERRIPROX (défériprone)
Medicine
- Posted on 24/10/2018 - Mis à jour le 12/6/2019
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BRINEURA (cerliponase alfa)
Medicine
- Posted on 24/10/2018 - Mis à jour le 12/6/2019
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DELURSAN (acide ursodésoxycholique)
Medicine
- Posted on 24/10/2018 - Mis à jour le 12/6/2019
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VOTUBIA (evérolimus)
Medicine
- Posted on 12/09/2019
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RAVICTI (phénylbutyrate de glycérol)
Medicine
- Posted on 05/09/2019
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CYSTADROPS (mercaptamine (chlorhydrate de))
Medicine
- Posted on 04/05/2018 - Mis à jour le 12/6/2019
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FLUCORTAC (fludrocortisone (acétate de))
Medicine
- Posted on 13/10/2022
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CAYSTON (aztréonam lysine/ lysine (aztréonam de))
Medicine
- Posted on 02/05/2018 - Mis à jour le 12/6/2019
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EXJADE (déférasirox)
Medicine
- Posted on 12/04/2018 - Mis à jour le 12/6/2019
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BESPONSA (inotuzumab ozogamicine)
Medicine
- Posted on 10/10/2022
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HYQVIA (immunoglobuline humaine normale (plasmatique))
Medicine
- Posted on 18/12/2023
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KOVALTRY (octocog alfa)
Medicine
- Posted on 29/03/2018 - Mis à jour le 12/6/2019
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REVESTIVE (teduglutide)
Medicine
- Posted on 21/05/2024
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